Duchenne muscular dystrophy (DMD) has gained recent attention. New symptom management and gene therapy treatments are at the forefront of DMD research. DMD is a genetic disease characterized by progressive muscle degeneration and weakness mainly affecting boys.
Building a national registry where all patient characteristics are identified is one of the most important tools that will aid in DMD research. Also, improving patient’s quality of life must be emphasized, which will include educating families and providing quality care to patients.