Anna is from England and recently finished her undergraduate degree. She has an interest in medicine and enjoys writing. In her spare time she likes to cook, hike, and hang out with cats.
A drug called Kineret has been approved by the European Commission in 28 European countries for the treatment of both adult-onset and juvenile-onset Still’s disease, reports Check Orphan. Still’s disease…
The University of Maryland has just published a press release after a researcher working at the university made several new discoveries about the bacteria that causes Lyme disease. Lyme disease…
Pfizer has just begun a medical trial for a potential gene therapy treatment for Duchenne muscular dystrophy, and the first patient has been dosed. Click here to read the original…
A $5 million charitable donation from the Isabella Santos Foundation has been committed to the Atrium Health’s Levine Children’s Hospital, reports FinacialContent. It will be used to establish The Isabella…
Researchers have found that forms of certain genes can influence how successful a blood and marrow transplant is, reports Roswell Park. This has important implications for understanding patient outcomes and…
An online patient survey has found that 96% of pulmonary fibrosis patients, and 93% of cystic fibrosis patients, support being able to monitor their lung function at home between visits…
There is a growing consensus that patients need to be more included in the medical field, reports PCMA Convene. Over the last ten years increasing numbers of organisations have moved…
The country singer, songwriter Gavin DeGraw has released a video to raise awareness for pancreatic cancer as part of an on-going campaign by the Lustgarten Foundation, reports PR Newswire. In…
Michael Conway, 51, was diagnosed with Adrenoleukodystrophy (ALD) two years ago. Since then, he has been raising awareness for the rare and potentially life-shortening condition. He wants to let people…
The U.S. Food and Drug Administration (FDA) have just approved a drug called Afinitor DISPERZ for treating tuberous sclerosis complex-associated partial onset seizures, reports PR Newswire. This makes it the…
A drug being developed to treat chronic kidney disease in Alport syndrome is showing promising results in patients in an on-going phase 2 clinical trial. Patients have shown an increase…
Research into graft-versus-host-disease (GVHD), a condition that can occur after bone marrow transplants, has yielded promising results. A study, reported by BrightSurf, found that a particular group of microRNA molecules involved…
In an effort to better understand patient experiences, researchers at the Massachusetts General Hospital are surveying people with lysosomal storage diseases about how they view their treatments, reports CheckOrphan. The…
Patients with sickle cell disease often face stigma about their need for pain medication because care providers are suspicious of drug abuse, reports The Dallas Post Tribune. Although this is…
Patients with a form of scleroderma called systemic sclerosis are particularly susceptible to developing high blood pressure in their heart and lungs, also known as pulmonary hypertension. A new study…
A recent study has found that reaching a correct diagnosis can be extremely challenging for people with mitochondrial disease, reports MedicalMalpractise. Patients are likely to have to undergo numerous different…
A new treatment under development has produced promising results in patients with blood cancers and is now being tested in inherited metabolic disorders, reports Financial Buzz. Inherited metabolic disorders are…
A class of drug called proton pump inhibitors (PPIs) that are used to treat acid reflux and heartburn have been linked to an increased risk of stomach cancer for some…
A drug being developed to treat cystic fibrosis has just been granted Fast Track Designation by the US Food and Drug Administration (FDA), reports PR Newswire. This shows that previous…
A new study looking at a test used to diagnose narcolepsy has found that it often produces inconsistent results for the same patients, reports Sleep Review. This highlights a current…
Peter Kay, a British comedian and actor, organised a screening of four episodes of his hit TV series Car Share in order to raise awareness and donations for a charity…
A new drug called Altemia is being developed to treat sickle cell diseases in children, reports BioPortfolio. It has recently been awarded Orphan Drug designation in both the United States…
Researchers at Northern Arizona University (NAU) are using microbial sequencing to better understand the causes of airway inflammatory diseases, including chronic rhinosinutsitis and cystic fibrosis. They hope that by studying…
A potential treatment of pulmonary infection for patients with cystic fibrosis (CF) and chronic obstructive pulmonary disease (COPD) has just been awarded U.S. patent status, reports Medicalxpress. Dr Daniel Hassett, a researcher…
Researchers at Northwestern University (NU) have published research showing that changes in the brain causing spinocerebellar ataxia type 1 (SCA1) occur at a younger age than previously thought, reports NeuroscienceNews.…
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